Post by Parexel

The conversations at World Orphan Drug Congress USA highlighted the growing momentum across the rare disease landscape. Over the past few days, our team shared perspectives on some of the field’s most pressing topics, from global development strategies and clinical trial feasibility to the role of genetic counseling and emerging digital technologies in rare disease research. What stood out most was the shared commitment among sponsors, regulators, patient advocates and industry partners to finding new ways to advance development and improve access for rare disease communities. Thank you to everyone who joined our sessions, visited our booth and shared insights throughout the event. We look forward to continuing these important conversations and helping advance innovative therapies for rare disease communities around the world. #WODC #WODC2026 #RareDisease #OrphanDrugDevelopment #ClinicalResearch #PatientsFirst