Post by Drug Discovery News

Researchers validate AGTC #GeneTherapy in #canine #model of X-linked #RetinitisPigmentosa #Subretinal #transgene admin corrected rod-cone #opsin mislocalization. Informed dosing of Phase 1/2 #ClinicalTrials https://lnkd.in/gyDCaX3 #XLRP #RareDiseases #ophthalmology Scheie Eye Institute University of Pennsylvania School of Veterinary Medicine Finn Partners