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The FDA has approved ๐„๐ญ๐ฎ๐ฏ๐ž๐ญ๐ข๐๐ข๐ ๐ž๐ง๐ž ๐š๐ฎ๐ญ๐จ๐ญ๐ž๐ฆ๐œ๐ž๐ฅ, the first gene therapy for ๐–๐ข๐ฌ๐ค๐จ๐ญ๐ญ-๐€๐ฅ๐๐ซ๐ข๐œ๐ก ๐ฌ๐ฒ๐ง๐๐ซ๐จ๐ฆ๐ž for pediatric patients aged 6 months and older and adults. โฃ โฃ Using a patientโ€™s own corrected stem cells, it delivers lasting clinical benefit, reducing infections and bleeding significantly. โฃ โฃ A major step forward in gene therapy, regulatory innovation, and hope for patients lacking matched donors.โฃ โฃ #FDA #GeneTherapy #WiskottAldrichSyndrome #RareDisease #StemCellTherapy #Immunology #Pediatrics #DrugApproval

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