Post by AZAFAROS B.V.
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The rare disease community will meet in Tucson, Arizona this weekend to discuss therapeutics, newborn screening, and developments in Niemann-Pick type C disease (#NPC) research at the annual Ara Parseghian Medical Research Fund conference. Chris Freitag, Chief Medical Officer at AZAFAROS B.V., will attend in person and give a poster presentation about our ongoing Phase 3 (#NAVIGATE) study investigating nizubaglustat in NPC, as well as in #GM1 and #GM2 gangliosidoses patients. Dr Freitag will also be available to talk with patient families, scientists and clinicians about our studies and clinical progress at the conference, which focuses on basic, translational clinical research towards a greater understanding and a cure for NPC. Looking forward to connecting with families and there! #NPC, #Parseghianfund, #navigate, #nizubaglustat, #clinicaltrials, #patientadvocacy, #drugdevelopment